Causes: Birth Defects & Genetic Diseases Research, Brain Disorders Research, Health, Pediatrics Research, Voluntary Health Associations & Medical Disciplines

Mission: Because Canavan Disease is considered an "orphan disease, " research to find a cure receives little public funding. Research is extremely dependent on our fundraising efforts. This means that the children born with devastating disease will not be cured unless we and similar organizations initiate, identify, and fund the necessary research.

Results: The first treatment, gene therapy, made history when it created the growth of myelin in the children's brains. Every single child who was treated with the gene therapy has experienced a better quality of life, the end of degeneration in the brain, and greater awareness of the world.