Causes: Down Syndrome Research, Health

Mission: To improve the lives of individuals with pku and pursue a cure.

Programs: Awarded $423,600 in our research program to research projects aimed at improving pku treatment and finding a cure.

the alliance engaged federal stakeholders on the importance of new treatments for pku including holding a patient engagement meeting with the fda on a possible new therapy to treat pku.

the alliance launched the international pku patient registry.

advocacy and all other programs aimed at furthering our mission.